Résultat correspond à votre recherche
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Revolutionising healing: Gene Editing's breakthrough against sickle cell disease.
Annarita Miccio
Source : Blood Rev
2024 mar 7
Pmid / DOI: 38493007
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Annarita Miccio
Source : Mol Ther Nucleic Acids
2023 déc 12
Pmid / DOI: 38034032
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Sickle Cell Disease: From Genetics to Curative Approaches.
Giulia Hardouin, Marina Cavazzana, Annarita Miccio
Source : Annu Rev Genomics Hum Genet
2023 aoû 25
Pmid / DOI: 37624668
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Mégane Brusson, Anne Chalumeau, Pierre Martinucci, Oriana Romano, Tristan Felix, Sophie Ramadier, Marina Cavazzana, Annarita Miccio
Source : Mol Ther Nucleic Acids
2023 mar 22
Pmid / DOI: 37090420
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Giulia Hardouin, Panagiotis Antoniou, Pierre Martinucci, Tristan Felix, Marina Cavazzana, Annarita Miccio
Source : Blood
2023 mar 9
Pmid / DOI: 36508706
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Letizia Fontana, Annarita Miccio , Panagiotis Antoniou
Source : Genes (Basel)
2023 fév 25
Pmid / DOI: 36980849
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Panagiotis Antoniou, Giulia Hardouin, Pierre Martinucci, Giacomo Frati, Tristan Felix, Anne Chalumeau, Letizia Fontana, Jeanne Martin, Mégane Brusson, Vincent Abramowski, Jean-Pierre De Villartay, Marina Cavazzana, Oriana Romano, Annarita Miccio
Source : Nat Commun
2022 nov 4
Pmid / DOI: 36333351
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CRISPRthripsis: The Risk of CRISPR/Cas9-induced Chromothripsis in Gene Therapy.
Mégane Brusson, Annarita Miccio
Source : Stem Cells Transl Med
2022 oct 21
Pmid / DOI: 36048170
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Long-term outcomes of lentiviral gene therapy for the β-hemoglobinopathies: the HGB-205 trial.
Anne Chalumeau, Adeline DENIS, Bénédicte Neven, Emmanuelle SIX, Annarita Miccio , Marina Cavazzana
Source : Nat Med
2022 jan 24
Pmid / DOI: 35075288
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Novel genome-editing-based approaches to treat motor neuron diseases: Promises and challenges.
Annarita Miccio , Panagiotis Antoniou, Sorana CIURA, Edor Kabashi
Source : Mol Ther
2022 jan 5
Pmid / DOI: 33823304
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Combination of lentiviral and genome editing technologies for the treatment of sickle cell disease.
Sophie Ramadier, Anne Chalumeau, Tristan Felix, Giacomo Frati, Mégane Brusson, Marina Cavazzana, Vasco Meneghini, Annarita Miccio
Source : Mol Ther
2022 jan 5
Pmid / DOI: 34418541
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Fetal hemoglobin rescues ineffective erythropoiesis in sickle cell disease.
Michael Dussiot, Giacomo Frati, Annarita Miccio
Source : Haematologica
2021 oct 1
Pmid / DOI: 32855279
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Anne Chalumeau, Annarita Miccio
Source : Blood Adv
2021 mar 9
Pmid / DOI: 33635334
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Genome editing approaches to β-hemoglobinopathies.
Mégane Brusson, Annarita Miccio
Source : Prog Mol Biol Transl Sci
2021 mar 1
Pmid / DOI: 34175041
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Genome Editing for β-Hemoglobinopathies: Advances and Challenges.
Giacomo Frati, Annarita Miccio
Source : J Clin Med
2021 jan 28
Pmid / DOI: 33525591