Filter Filter Par date Date de début Date de fin Par équipe Michel Polak Alessandra Pierani Patrick Revy & Erika Brunet Sigolène Meilhac Laurent Abel Jeanne Amiel et Laurence Legeai‑Mallet Antonio Rausell Isabelle André Vincent Cantagrel Jean-Laurent Casanova Nadine Cerf-Bensussan Yanick Crow Olivier Hermine & Thiago Trovati Maciel Alain Hovnanian Edor Kabashi Sylvain Latour Valérie Cormier-Daire Mickaël Ménager Gaël Ménasché et Fernando Sepulveda Annarita Miccio Frédéric Rieux-Laucat Agnès Rötig Jean-Michel Rozet Sophie Saunier et Corinne Antignac Matias Simons Nathalie Boddaert Sabine Sarnacki et Isabelle Bloch Yves Ville Anne DUMAINE Patrick Nitschké Corinne Cordier Meriem Garfa-Traoré Sylvie Fabrega Marie-Alexandra Alyanakian Sophie Berissi Chiara Guerrera Pierre David Nathalie Lefort Claude Besmond Marcelo Simon Sola LEAT Nathalie Boddaert Travail en collaboration : Unité de Recherche clinique-Centre d’investigation clinique (URC-CIC) Travail en collaboration : Département de Biothérapie, Centre d'Investigation Clinique pour les Thérapies Innovantes Salma Kotti Nicolas Garcelon Mickaël Ménager Michela Deleidi Annarita Miccio Annarita Miccio Jean Michel Rozet Sara Bizzotto Elodie Bal Bana Jabri Hossein Khonsari Karim Wahbi Lucile Couronné Denis Jabaudon, Thomas Blauwblomme et Rima Nabbout Bana Jabri Céline GRECO Filter Reset Résultat correspond à votre recherche Publications A prime editing strategy to rewrite the γ-globin promoters and reactivate... Publications Dissecting the epigenetic regulation of the fetal hemoglobin genes to unravel... Publications Revolutionising healing: Gene Editing's breakthrough against sickle cell... Publications Progress and harmonization of gene editing to treat human diseases: Proceeding... Publications Sickle Cell Disease: From Genetics to Curative Approaches. Publications Novel lentiviral vectors for gene therapy of sickle cell disease combining... Publications Adenine base editor-mediated correction of the common and severe IVS1-110... Publications Epigenetic Regulation of β-Globin Genes and the Potential to Treat Hemoglobinopathies... Publications Base-editing-mediated dissection of a γ-globin cis-regulatory element... Publications CRISPRthripsis: The Risk of CRISPR/Cas9-induced Chromothripsis in Gene... Publications Long-term outcomes of lentiviral gene therapy for the β-hemoglobinopathies:... Publications Combination of lentiviral and genome editing technologies for the treatment... Publications Novel genome-editing-based approaches to treat motor neuron diseases: Promises... Publications Fetal hemoglobin rescues ineffective erythropoiesis in sickle cell dis... Publications Correction of β-thalassemia by CRISPR/Cas9 editing of the α-globin locus... Pagination Page courante 1 Page 2 Page 3 Page Suivant Dernière page Newsletter Découvertes, avancées, portraits... retrouvez l'actualité de la recherche et les dernières innovations médicales. Votre email Valider Politique de confidentialité des données