20 Résultats correspondent à votre recherche
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Novel genome-editing-based approaches to treat motor neuron diseases: Promises and challenges.
Annarita Miccio , Panagiotis Antoniou, Sorana CIURA, Edor Kabashi
Source : Mol Ther
2022 jan 5
Pmid : 33823304
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GATA Factor-Mediated Gene Regulation in Human Erythropoiesis.
Oriana Romano, Tristan Felix, Vasco Meneghini, Chiara Antoniani, Annarita Miccio
Source : iScience
2020 avr 24
Pmid : 32283524
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Annarita Miccio
Source : Sci Adv
2020 mar 5
Pmid : 32095533
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Leslie WEBER, Giacomo Frati, Tristan Felix, Giulia Hardouin, Clara Wollenschlaeger, Vasco Meneghini, Anne Chalumeau, Marina Cavazzana, Annarita Miccio
Source : Sci Adv
2020 fév 1
Pmid : 32917636
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GATA factor transcriptional activity: Insights from genome-wide binding profiles.
Annarita Miccio , Oriana Romano
Source : IUBMB Life
2019 déc 16
Pmid : 31574210
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Lentiviral and genome-editing strategies for the treatment of β-hemoglobinopathies.
Marina Cavazzana, Annarita Miccio
Source : Blood
2019 déc 13
Pmid : 31467062
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Gene therapy of hemoglobinopathies: progress and future challenges.
Marina Cavazzana
Source : Hum. Mol. Genet.
2019 déc 13
Pmid : 31322165
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Annarita Miccio
Source : Mol. Ther.
2019 déc 11
Pmid : 30424953
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An Optimized Lentiviral Vector Efficiently Corrects the Human Sickle Cell Disease Phenotype.
Annarita Miccio
Source : Mol Ther Methods Clin Dev
2019 nov 20
Pmid : 30140714
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Gene therapy targeting haematopoietic stem cells for inherited diseases: progress and challenges.
Annarita Miccio , Emmanuelle SIX, Isabelle André, Marina Cavazzana
Source : Nat Rev Drug Discov
2019 nov 8
Pmid : 30858502
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Marina Cavazzana
Source : Haematologica
2019 sep 20
Pmid : 31537695
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Chantal LAGRESLE-PEYROU, Oriana Romano, Tristan Felix, Marianne DELVILLE, Isabelle André, Marina Cavazzana, Annarita Miccio , Tristan Felix
Source : Haematologica
2019 juil 8
Pmid : 29472357
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Annarita Miccio
Source : Stem Cells Transl Med
2019 juin 27
Pmid : 29080249
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Induction of fetal hemoglobin synthesis by CRISPR/Cas9-mediated editing of the human β-globin locus.
Annarita Miccio , Tristan Felix
Source : Blood
2019 mai 14
Pmid : 29519807
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Annarita Miccio
Source : Sci Rep
2017 mar 8
Pmid : 27095295