Présentation
Publications scientifiques
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2025Journal (source)Nucleic Acids ResearchDissecting the epigenetic regulation of the fetal hemoglobin genes to unravel...
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2023Journal (source)Mol Ther Nucleic Acids
Novel lentiviral vectors for gene therapy of sickle cell disease combining ge...
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2023Journal (source)Blood
Adenine base editor-mediated correction of the common and severe IVS1-110 (G>...
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2022Journal (source)Nat Commun
Base-editing-mediated dissection of a γ-globin cis-regulatory element for the...
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2022Journal (source)Mol Ther
Combination of lentiviral and genome editing technologies for the treatment o...
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2020Journal (source)iScience
GATA Factor-Mediated Gene Regulation in Human Erythropoiesis.
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2019Journal (source)Haematologica
Plerixafor enables safe, rapid, efficient mobilization of hematopoietic stem ...
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2018Journal (source)Mol. Ther.
Optimization of CRISPR/Cas9 Delivery to Human Hematopoietic Stem and Progenit...
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Journal (source)Mol Ther Methods Clin Dev
An Optimized Lentiviral Vector Efficiently Corrects the Human Sickle Cell Dis...
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2018Journal (source)Blood
Induction of fetal hemoglobin synthesis by CRISPR/Cas9-mediated editing of th...