Présentation
Publications scientifiques
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2025Journal (source)Nucleic Acids Research
Dissecting the epigenetic regulation of the fetal hemoglobin genes to unravel...
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2023Journal (source)Mol Ther Nucleic Acids
Novel lentiviral vectors for gene therapy of sickle cell disease combining ge...
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2023Journal (source)Blood
Adenine base editor-mediated correction of the common and severe IVS1-110 (G>...
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2022Journal (source)Nat Commun
Base-editing-mediated dissection of a γ-globin cis-regulatory element for the...