Highly Efficient Ex Vivo Correction of COL7A1 through Ribonucleoprotein-Based CRISPR/Cas9 and Homology-Directed Repair to Treat Recessive Dystrophic Epidermolysis Bullosa
Berthault C,Gaucher S,Gouin O,Schmitt A,Chen M,Woodley D,Titeux M,Hovnanian A,Izmiryan A
Source :
2024 Jun 1
Pmid / DOI:
10.1016/j.jid.2023.10.035