Successful RAG1-SCID gene therapy depends on the level of RAG1 expression.
Pike-Overzet K, Baum C, Bredius RG, Cavazzana M, Driessen GJ, Fibbe WE, Gaspar HB, Hoeben RC, Lagresle-Peyrou C, Lankester A, Meij P, Schambach A, Thrasher A, Van Dongen JJ, Zwaginga JJ, Staal FJ.
    Source :
    
                  
            J Allergy Clin Immunol
      
              
  
    
                  
            2014 juil 1
      
              
  
      Pmid / DOI:
      
                    
            25117803