Successful RAG1-SCID gene therapy depends on the level of RAG1 expression.

Pike-Overzet K, Baum C, Bredius RG, Cavazzana M, Driessen GJ, Fibbe WE, Gaspar HB, Hoeben RC, Lagresle-Peyrou C, Lankester A, Meij P, Schambach A, Thrasher A, Van Dongen JJ, Zwaginga JJ, Staal FJ.

Source : J Allergy Clin Immunol

2014 juil 1

Pmid / DOI: 25117803