Successful RAG1-SCID gene therapy depends on the level of RAG1 expression.
Pike-Overzet K,Baum C,Bredius R,Cavazzana M,Driessen G,Fibbe W,Gaspar H,Hoeben R,Lagresle-Peyrou C,Lankester A,Meij P,Schambach A,Thrasher A,Van Dongen J,Zwaginga J,Staal F
Source :
J Allergy Clin Immunol
2014 Jun 26
Pmid / DOI:
25117803