Annarita MICCIO
Chromatin and gene regulation during development
Team
Scientific Publications
-
2025Journal (source)BloodA prime editing strategy to rewrite the γ-globin promoters and reactivate fet...
-
2025Journal (source)Nucleic Acids Research
Dissecting the epigenetic regulation of the fetal hemoglobin genes to unravel...
-
2023Journal (source)Mol Ther Nucleic Acids
Novel lentiviral vectors for gene therapy of sickle cell disease combining ge...
-
2023Journal (source)Blood
Adenine base editor-mediated correction of the common and severe IVS1-110 (G>...
-
2022Journal (source)Nat Commun
Base-editing-mediated dissection of a γ-globin cis-regulatory element for the...
-
2022Journal (source)Nat Med
Long-term outcomes of lentiviral gene therapy for the β-hemoglobinopathies: t...
-
2022Journal (source)Mol Ther
Combination of lentiviral and genome editing technologies for the treatment o...
-
2021Journal (source)Haematologica
Fetal hemoglobin rescues ineffective erythropoiesis in sickle cell disease.
-
2021Journal (source)Blood Adv
Correction of β-thalassemia by CRISPR/Cas9 editing of the α-globin locus in h...
