Reverse-Transcriptase Inhibitors in the Aicardi–Goutières Syndrome.
Rice G,Meyzer C,Bouazza N,Hully M,Boddaert N,Semeraro M,Zeef L,Rozenberg F,Bondet V,Duffy D,Llibre A,Baek J,Sambe M,Henry E,Jolaine V,Barnerias C,Barth M,Belot A,Cances C,Debray F,Doummar D,Frémond M,Kitabayashi N,Lepelley A,Levrat V,Melki I,Meyer P,Nougues M,Renaldo F,Rodero M,Rodriguez D,Roubertie A,Seabra L,Uggenti C,Abdoul H,Treluyer J,Desguerre I,Blanche S,Crow Y
Source :
N Engl J Med
2018 Dec 20
Pmid / DOI:
30566312