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Chantal LAGRESLE-PEYROU, Laëtitia Kermasson, Patrick Nitschké, Marina Cavazzana, Alain Fischer, Jean-Pierre De Villartay, Patrick Revy
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The BLNK adaptor protein has a nonredundant role in human B-cell differentiation.
Chantal LAGRESLE-PEYROU, Hanem SADEK, Marina Cavazzana
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Successful RAG1-SCID gene therapy depends on the level of RAG1 expression.
Marina Cavazzana, Chantal LAGRESLE-PEYROU
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Chantal LAGRESLE-PEYROU, Marina Cavazzana
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Isabelle André, Laura SIMONS, Kuiying MA, Marina Cavazzana
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Gene Therapy with Hematopoietic Stem Cells: The Diseased Bone Marrow's Point of View.
Marina Cavazzana, Chantal LAGRESLE-PEYROU
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Single-cell analysis reveals the continuum of human lympho-myeloid progenitor cells.
Emmanuelle SIX
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Outcomes following gene therapy in patients with severe Wiskott-Aldrich syndrome.
Emmanuelle SIX, Alain Fischer, Marina Cavazzana
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Julien ZUBER, Olivia Boyer, Bénédicte Neven, Romain Levy, Baptiste LAMARTHÉE, Michael Dussiot, Isabelle André, Marina Cavazzana
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Emmanuelle SIX, Marianne DELVILLE, Julien ZUBER, Bénédicte Neven, Nadine CERF-BENSUSSAN , Frédéric Rieux-Laucat, Marina Cavazzana, Isabelle André
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