Résultat de recherche

Sickle Cell Disease: From Genetics to Curative Approaches.

Giulia Hardouin, Marina Cavazzana, Annarita Miccio

Source :

Pmid / DOI:

Adenine base editor-mediated correction of the common and severe IVS1-110 (G>A) β-thalassemia mutation.

Giulia Hardouin, Panagiotis Antoniou, Pierre Martinucci, Tristan Felix, Marina Cavazzana, Annarita Miccio

Source :

Pmid / DOI:

Epigenetic Regulation of β-Globin Genes and the Potential to Treat Hemoglobinopathies through Epigenome Editing.

Letizia Fontana, Annarita Miccio , Panagiotis Antoniou

Source :

Pmid / DOI:

CRISPRthripsis: The Risk of CRISPR/Cas9-induced Chromothripsis in Gene Therapy.

Mégane Brusson, Annarita Miccio

Source :

Pmid / DOI:

Combination of lentiviral and genome editing technologies for the treatment of sickle cell disease.

Sophie Ramadier, Anne Chalumeau, Tristan Felix, Giacomo Frati, Mégane Brusson, Marina Cavazzana, Vasco Meneghini, Annarita Miccio

Source :

Pmid / DOI:

Fetal hemoglobin rescues ineffective erythropoiesis in sickle cell disease.

Michael Dussiot, Giacomo Frati, Annarita Miccio

Source :

Pmid / DOI:

Correction of β-thalassemia by CRISPR/Cas9 editing of the α-globin locus in human hematopoietic stem cells.

Anne Chalumeau, Annarita Miccio

Source :

Pmid / DOI:

Base and Prime Editing Technologies for Blood Disorders.

Panagiotis Antoniou, Annarita Miccio , Mégane Brusson

Source :

Pmid / DOI:

Genome Editing for β-Hemoglobinopathies: Advances and Challenges.

Giacomo Frati, Annarita Miccio

Source :

Pmid / DOI:

A Genome Editing System for Therapeutical Targeting of Stem Cells.

Giacomo Frati, Annarita Miccio

Source :

Pmid / DOI: