Presentation
Scientific Publications
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2025Journal (source)Nucleic Acids ResearchDissecting the epigenetic regulation of the fetal hemoglobin genes to unravel...
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2023Journal (source)BloodAdenine base editor-mediated correction of the common and severe IVS1-110 (G>...
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2023Journal (source)Mol Ther Nucleic AcidsNovel lentiviral vectors for gene therapy of sickle cell disease combining ge...
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2022Journal (source)Nat CommunBase-editing-mediated dissection of a γ-globin cis-regulatory element for the...