Presentation
Resources & publications
-
2019Journal (source)BloodInduction of fetal hemoglobin synthesis by CRISPR/Cas9-mediated editing of th...
-
2019Journal (source)Haematologica
Plerixafor enables safe, rapid, efficient mobilization of hematopoietic stem ...
-
2020Journal (source)iScience
GATA Factor-Mediated Gene Regulation in Human Erythropoiesis.
-
2022Journal (source)Nat Commun
Base-editing-mediated dissection of a γ-globin cis-regulatory element for the...
-
2023Journal (source)Mol Ther Nucleic Acids
Novel lentiviral vectors for gene therapy of sickle cell disease combining ge...
-
2023Journal (source)Blood
Adenine base editor-mediated correction of the common and severe IVS1-110 (G>...
-
2022Journal (source)Mol Ther
Combination of lentiviral and genome editing technologies for the treatment o...