Résultat de recherche

Gene therapy targeting haematopoietic stem cells for inherited diseases: progress and challenges.

Annarita Miccio , Emmanuelle SIX, Isabelle André, Marina Cavazzana

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Optimization of CRISPR/Cas9 Delivery to Human Hematopoietic Stem and Progenitor Cells for Therapeutic Genomic Rearrangements.

Annarita Miccio

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An Optimized Lentiviral Vector Efficiently Corrects the Human Sickle Cell Disease Phenotype.

Annarita Miccio

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Induction of fetal hemoglobin synthesis by CRISPR/Cas9-mediated editing of the human β-globin locus.

Annarita Miccio , Tristan Felix

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Concise Review: Epigenetic Regulation of Hematopoiesis: Biological Insights and Therapeutic Applications.

Annarita Miccio

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Transcriptional, epigenetic and retroviral signatures identify regulatory regions involved in hematopoietic lineage commitment.

Annarita Miccio

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Dynamic Transcriptional and Epigenetic Regulation of Human Epidermal Keratinocyte Differentiation.

Annarita Miccio

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Genome-Wide Definition of Promoter and Enhancer Usage during Neural Induction of Human Embryonic Stem Cells.

Annarita Miccio

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Nup153 and Nup98 bind the HIV-1 core and contribute to the early steps of HIV-1 replication.

Annarita Miccio

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Deletion of the LTR enhancer/promoter has no impact on the integration profile of MLV vectors in human hematopoietic progenitors.

Annarita Miccio

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Lentiviral vector integration in the human genome induces alternative splicing and generates aberrant transcripts.

Annarita Miccio

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